CGTBiologicstaleNational Center for Research Re…Phase 1
Ornithine transcarbamylase vector (Ornithine transcarbamylase vector)
Amino Acid Metabolism, Inborn Errors · Amino Acid Metabolism, Inborn Errors
#AminoAcidMetabolismInbornErrors#CGT#Phase1#세포유전치료#CAR-T+4
임상시험 1상태 ACTIVE