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ADC 1068 · Antibody 5456 · CGT 2744 · 다음 갱신 D-10 · 마지막 7월 13일

인기최근 업데이트큐레이션임상 많은갱신 필요ORR최신Phase 3FDA승인프로그램 4,162개
CGTAAVBiologicstaleMeiraGTx UK II LtdPreclinical

AAV OPTIRPE65 (AAV OPTIRPE65)

Leber Congenital Amaurosis (LCA); Eye Diseases · Leber Congenital Amaurosis (LCA)

#LeberCongenitalAmaurosisLCA#CGT#Preclinical#세포유전치료#CAR-T+3
임상시험 1상태 ACTIVE
CGTAAVBiologicstaleREGENXBIO Inc.Phase 2

AAV directed hLDLR gene therapy (AAV directed hLDLR gene therapy)

Homozygous Familial Hypercholesterolemia (HoFH) · Homozygous Familial Hypercholesterolemia

#HomozygousFamilialHypercholester#CGT#Phase2#세포유전치료#CAR-T+2
임상시험 1상태 DISCONTINUED
CGTAAVBiologicstaleMeiraGTx, LLCPhase 2

AAV-GAD High Dose (AAV-GAD High Dose)

Parkinson's Disease · Parkinson's Disease

#ParkinsonsDisease#CGT#Phase2#세포유전치료#CAR-T+2
임상시험 1상태 ACTIVE
CGTAAVBiologicstaleMeiraGTx, LLCPhase 2

AAV-GAD Low Dose (AAV-GAD Low Dose)

Parkinson's Disease · Parkinson's Disease

#ParkinsonsDisease#CGT#Phase2#세포유전치료#CAR-T+2
임상시험 1상태 ACTIVE
CGTAAVBiologicstaleUniversity of OxfordPhase 2

AAV-mediated REP1 gene replacement (AAV-mediated REP1 gene replacement)

Choroideremia · Choroideremia

#Choroideremia#CGT#Phase2#세포유전치료#CAR-T+2
임상시험 1상태 ACTIVE
CGTAAVBiologicstaleMark TuszynskiPhase 1

AAV2-BDNF Gene Therapy (AAV2-BDNF Gene Therapy)

Alzheimer's Disease; Mild Cognitive Impairment · Alzheimer's Disease

#AlzheimersDisease#CGT#Phase1#세포유전치료#CAR-T+3
임상시험 1상태 RECRUITING
CGTAAVBiologicstaleMeiraGTx, LLCPhase 2

AAV2-hAQP1 (AAV2-hAQP1)

Grade 2 and 3 Late Xerostomia Caused by Radiotherapy for Cancers of the Upper Aerodigestive Tract, Excluding the Paroti… · Grade 2 and 3 Late Xerostomia Caused by

#Grade2and3LateXerostomiaCausedby#CGT#Phase2#세포유전치료#CAR-T+3
임상시험 1상태 ACTIVE
CGTAAVBiologicstaleMeiraGTx, LLCPhase 2

AAV2-hAQP1 Concentration 1 (AAV2-hAQP1 Concentration 1)

Grade 2 and 3 Late Xerostomia Caused by Radiotherapy for Cancers of the Upper Aerodigestive Tract, Excluding the Paroti… · Grade 2 and 3 Late Xerostomia Caused by

#Grade2and3LateXerostomiaCausedby#CGT#Phase2#세포유전치료#CAR-T+3
임상시험 1상태 RECRUITING
CGTAAVBiologicstaleMeiraGTx, LLCPhase 2

AAV2-hAQP1 Concentration 2 (AAV2-hAQP1 Concentration 2)

Grade 2 and 3 Late Xerostomia Caused by Radiotherapy for Cancers of the Upper Aerodigestive Tract, Excluding the Paroti… · Grade 2 and 3 Late Xerostomia Caused by

#Grade2and3LateXerostomiaCausedby#CGT#Phase2#세포유전치료#CAR-T+3
임상시험 1상태 RECRUITING
CGTAAVBiologicstaleMeiraGTx, LLCPhase 2

AAV2-hAQP1 Concentration 3 (AAV2-hAQP1 Concentration 3)

Grade 2 and 3 Late Xerostomia Caused by Radiotherapy for Cancers of the Upper Aerodigestive Tract, Excluding the Paroti… · Grade 2 and 3 Late Xerostomia Caused by

#Grade2and3LateXerostomiaCausedby#CGT#Phase2#세포유전치료#CAR-T+3
임상시험 1상태 RECRUITING
CGTAAVBiologicstaleMeiraGTx, LLCPhase 2

AAV2-hAQP1 Concentration 4 (AAV2-hAQP1 Concentration 4)

Grade 2 and 3 Late Xerostomia Caused by Radiotherapy for Cancers of the Upper Aerodigestive Tract, Excluding the Paroti… · Grade 2 and 3 Late Xerostomia Caused by

#Grade2and3LateXerostomiaCausedby#CGT#Phase2#세포유전치료#CAR-T+3
임상시험 1상태 RECRUITING
CGTAAVBiologicstaleSpark Therapeutics, Inc.Phase 2

AAV2-hCHM (AAV2-hCHM)

Choroideremia; CHM (Choroideremia) Gene Mutations · Choroideremia

#Choroideremia#CGT#Phase2#세포유전치료#CAR-T+3
임상시험 1상태 ACTIVE
CGTAAVBiologicstaleeyeDNA TherapeuticsPhase 2

AAV2/5-hPDE6B (AAV2/5-hPDE6B)

Retinitis Pigmentosa · Retinitis Pigmentosa

#RetinitisPigmentosa#CGT#Phase2#세포유전치료#CAR-T+2
임상시험 1상태 DISCONTINUED
CGTAAVBiologicstaleMedical Research CouncilPhase 2

AAV2/8-HLP-FVIII-V3 (AAV2/8-HLP-FVIII-V3)

Hemophilia A · Hemophilia A

#HemophiliaA#CGT#Phase2#세포유전치료#CAR-T+2
임상시험 1상태 RECRUITING
CGTAAVBiologicstaleSpark Therapeutics, Inc.Phase 1

AAV8-hFIX19 (AAV8-hFIX19)

Hemophilia B · Hemophilia B

#HemophiliaB#CGT#Phase1#세포유전치료#CAR-T+2
임상시험 1상태 DISCONTINUED
CGTAAVBiologicstaleAspa TherapeuticsPhase 2

AAV9 BBP-812 (AAV9 BBP-812)

Canavan Disease · Canavan Disease

#CanavanDisease#CGT#Phase2#세포유전치료#CAR-T+2
임상시험 1상태 RECRUITING
CGTAAVBiologicstaleUnlimited Biotechnology LLCPhase 2

AAV9-Follistatin gene therapy (AAV9-Follistatin gene therapy)

Age-related Muscle Decline · Age-related Muscle Decline

#Age-relatedMuscleDecline#CGT#Phase2#세포유전치료#CAR-T+2
임상시험 1상태 RECRUITING
CGTAAVBiologicUniQure Biopharma B.V.Phase 2

AAV9-hSyn1-miGRIK2 (AAV9-hSyn1-miGRIK2)

Mesial Temporal Lobe Epilepsy · Mesial Temporal Lobe Epilepsy

#MesialTemporalLobeEpilepsy#CGT#Phase2#세포유전치료#CAR-T+2
임상시험 1상태 RECRUITING
CGTBiologicAkouos, Inc.Phase 2

AAVAnc80-hOTOF via Akouos Delivery Device (AAVAnc80-hOTOF via Akouos Delivery Device)

Sensorineural Hearing Loss, Bilateral · Sensorineural Hearing Loss, Bilateral

#SensorineuralHearingLossBilatera#CGT#Phase2#세포유전치료#CAR-T+4
임상시험 1상태 RECRUITING
CGTBiologicAkouos, Inc.Phase 2

AAVAnc80-hOTOF via Akouos Delivery Device and Precision Delivery Mechanism (AAVAnc80-hOTOF via Akouos Delivery Device and Precision Delivery Mechanism)

Sensorineural Hearing Loss, Bilateral · Sensorineural Hearing Loss, Bilateral

#SensorineuralHearingLossBilatera#CGT#Phase2#세포유전치료#CAR-T+4
임상시험 1상태 RECRUITING

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