CGTAAVBHOTFDACuratedFDABiologicSpark TherapeuticsHuman RPE65 cDNAApproved
voretigene neparvovec (Luxturna, AAV2-hRPE65v2, voretigene neparvovec-rzyl)
Inherited retinal dystrophy due to confirmed biallelic RPE65 mutations · RPE65 (AAV2)
#RPE65AAV2#CGT#Approved#FDA승인#바이오모아추천+5
임상시험 7상태 APPROVED